News & Videos
- UCSD's Dr. Adler Awarded $1.4M for stem cell research
- Young patient's skin cells used as a heart model
- Dr. Adler on the treatment of Danon Disease
- FDA clears Rocket Pharma's IND for RP-A501
- Rocket Pharmaceuticals Announces Preclinical Data for AAV-Based RP-A501, the First Investigational Gene Therapy Program for a Monogenic Heart Failure Syndrome
- Rocket Pharmaceuticals Announces Positive Updates from Phase 1 Clinical Trial of RP-A501 in Danon Disease
- Gene Therapy for Male Patients With Danon Disease Using RP-A501; AAV9.LAMP2B