News & Videos

•  UCSD's Dr. Adler Awarded $1.4M for stem cell research 
•  Young patient's skin cells used as a heart model
•  Dr. Adler on the treatment of Danon Disease
•  FDA clears Rocket Pharma's IND for RP-A501
• Rocket Pharmaceuticals Announces Preclinical Data for AAV-Based RP-A501, the First Investigational Gene Therapy Program for a Monogenic Heart Failure Syndrome
• Rocket Pharmaceuticals Announces Positive Updates from Phase 1 Clinical Trial of RP-A501 in Danon Disease
• Gene Therapy for Male Patients With Danon Disease Using RP-A501; AAV9.LAMP2B