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Adler Lab
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UCSD's Dr. Adler Awarded $1.4M fo
r stem cell research
Young patient's skin cells used as a heart model
Dr. Adler on the treatment of Danon Disease
FDA clears Rocket Pharma's IND for RP-A501
Rocket Pharmaceuticals Announces Preclinical Data for AAV-Based RP-A501, the First Investigational Gene Therapy Program for a Monogenic Heart Failure Syndrome
Rocket Pharmaceuticals Announces Positive Updates from Phase 1 Clinical Trial of RP-A501 in Danon Disease
Gene Therapy for Male Patients With Danon Disease Using RP-A501; AAV9.LAMP2B
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